Efficient correction of ABCA4 variants by CRISPR-Cas9 in hiPSCs derived from Stargardt disease patientsLaura Siles, Esther Pomares|Molecular Therapy — Nucleic Acids|2023Cited by 24
High-Efficiency CRISPR/Cas9-Mediated Correction of a Homozygous Mutation in Achromatopsia-Patient-Derived iPSCsLaura Siles, Esther Pomares|International Journal of Molecular Sciences|2023Cited by 8
Rescue of the disease-associated phenotype in CRISPR-corrected hiPSCs as a therapeutic approach for inherited retinal dystrophiesLaura Siles, Esther Pomares|Molecular Therapy — Nucleic Acids|2025Cited by 4