Both TALENs and CRISPR/Cas9 directly target the HBB IVS2–654 (C > T) mutation in β-thalassemia-derived iPSCs
Peng Xu(Directorate for Cultural Heritage), De‐Pei Liu(Chinese Academy of Medical Sciences & Peking Union Medical College), Xiuzhen Liu(Chinese Academy of Medical Sciences & Peking Union Medical College), Xiang Lv(Xinyang Agriculture and Forestry University), Cheng Li(Central South University), Yue Huang(Chinese Academy of Medical Sciences & Peking Union Medical College), Ying Tong(Renji Hospital), Tingting Wang(Central South University), Bo-yu Wang(Chinese Academy of Medical Sciences & Peking Union Medical College)
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