Gene Supplementation of MYO7A or activation of Myo7b for treatment of Usher syndrome 1B

David Manuel Mittas(University of Zurich), Elvir Bećirović(University of Zurich), Susanne Koch(LMU Klinikum), Olivier Mercey(University of Geneva), Stylianos Michalakis(LMU Klinikum), Jana Juhásová(Czech Academy of Sciences, Institute of Animal Physiology and Genetics), Virginie Hamel(University of Geneva), Andreas Wiest(LMU Klinikum), Taras Ardan(Czech Academy of Sciences, Institute of Animal Physiology and Genetics), Jan Wijnholds(Leiden University Medical Center), Andreas Klingl(Vienna Biocenter), Paul Guichard(University of Geneva), Zdeňka Ellederová(Czech Academy of Sciences, Institute of Animal Physiology and Genetics), Hermann Ammer(Ludwig-Maximilians-Universität München), Nanda Boon(Leiden University Medical Center), A. F. Kolesnikova(Charles University), Miroslav Veith(Charles University), Saskia Drutovič(Czech Academy of Sciences, Institute of Animal Physiology and Genetics), Štefan Juhás(Czech Academy of Sciences, Institute of Animal Physiology and Genetics), Ruslan Nyshchuk(Charles University), Verena Mehlfeld(Ludwig-Maximilians-Universität München), Martin Biel(Ludwig-Maximilians-Universität München), Thomas Heigl(University of Zurich), Manuel Fischer(University of Basel), Jan Motlík(Czech Academy of Sciences, Institute of Animal Physiology and Genetics), Paulina Deltuvaite(University of Zurich), Zoran Gavrilov(University of Zurich), Dina Otify(University of Zurich), Guelce Goekce(LMU Klinikum), Jennifer Gruenert(Vienna Biocenter), Franz Kynast(LMU Klinikum), Zbynek Stranak(Charles University), Klara Sonnie Hinrichsmeyer(University of Zurich), Jan Suchomski(University of Zurich), Pavel Kielkowski(LMU Klinikum)
bioRxiv (Cold Spring Harbor Laboratory)
July 3, 2026
Cited by 0


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