Selection of human hematopoietic stem cells bearing the intended functional edit by transient AND-gate reporters

Daniele Canarutto(Vita-Salute San Raffaele University), Luigi Naldini(IRCCS Ospedale San Raffaele), Angelo Amabile(Icahn School of Medicine at Mount Sinai), Martina Fiumara(The San Raffaele Telethon Institute for Gene Therapy), Gabriele Pelosi(The San Raffaele Telethon Institute for Gene Therapy), Giulia Schiroli(Xperi (United States)), Samuele Ferrari(Vita-Salute San Raffaele University), Deborah Cipria(The San Raffaele Telethon Institute for Gene Therapy), Chiara Gaddoni(The San Raffaele Telethon Institute for Gene Therapy), Pietro Genovese(Boston Children's Hospital), Bernhard Gentner(The San Raffaele Telethon Institute for Gene Therapy), Luisa Albano(The San Raffaele Telethon Institute for Gene Therapy), Angelica Varesi(The San Raffaele Telethon Institute for Gene Therapy), Erika Zonari(The San Raffaele Telethon Institute for Gene Therapy), Claudia Firrito(The San Raffaele Telethon Institute for Gene Therapy), Stefano Beretta(The San Raffaele Telethon Institute for Gene Therapy), Alfredo Silva(The San Raffaele Telethon Institute for Gene Therapy), Vigneshwaran Venkatesan(The San Raffaele Telethon Institute for Gene Therapy), Anna Villa(Institute of Genetic and Biomedical Research), Angelo Lombardo(Vita-Salute San Raffaele University), Kohei Shiroshita(The San Raffaele Telethon Institute for Gene Therapy)
Nature Biotechnology
June 1, 2026
Cited by 0


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