Prime editing of a pathogenic allele ameliorates seizure phenotypes in a GEFS mouse model
Lucas Kissling(University of Zurich), Gerald Schwank(ETH Zurich), Lukas Schmidheini(University of Zurich), Nicolas Mathis(University of Zurich), Péter István Kulcsár(University of Zurich), Hendrik Wildner, Konstantinos Kompotis, András Tálas(University of Zurich), Elina Andrea Villiger(University of Zurich), Desiree Boeck, Matteo Ranucci, Francesca Pietrafesa, Xinyue Zhao, Eleonora Ioannidi, Hanns Ulrich Zeilhofer(University of Zurich)
Cited by 0
Related Papers
In vivo adenine base editing of PCSK9 in macaques reduces LDL cholesterol levels
|Nature Biotechnology|2021|375
In vivo prime editing of a metabolic liver disease in mice
|Science Translational Medicine|2022|184
Predicting prime editing efficiency and product purity by deep learning
|Nature Biotechnology|2023|145