Lipid nanoparticle delivery of antisense gapmers attenuates pathology in a mouse model of facioscapulohumeral muscular dystrophy

Saeed Anwar(Shahjalal University of Science and Technology), Toshifumi Yokota(University of Alberta), Yusuke Echigoya(Nihon University), Darko Bosnakovski(Unknown), Abdullah Zia(University of Alberta), Karen Ying Tung Chan(University of British Columbia), Pieter R. Cullis(University of British Columbia), Umme Sabrina Haque(University of Alberta), Dominik Witzigmann(FPInnovations), Md Nur Ahad Shah(University of Alberta), Samuel L. Beck(University of Alberta), Michael Kyba(University of Minnesota), Kenji Rowel Q. Lim(Washington University in St. Louis), Rika Maruyama(University of Alberta), Hidenori Moriyama(Keio University)
Molecular Therapy
May 1, 2026
Cited by 0


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