A gene therapy strategy for Deoxyhypusine Synthase (DHPS) syndrome
Carolina Nunes Santo(University of California San Diego), Alysson R. Muotri(University of California San Diego), Teresa L. Mastracci(Indiana University Indianapolis), Qiaoyan Yang(Shenzhen University), Rebeca Blanch(University of California San Diego), Juliana Laze(New York University), Orrin Devinsky(New York University), Olin Konishi(New York University), Angela Dias(University of California San Diego), Mollie R. Shinkle(Indiana University – Purdue University Indianapolis), Chengzu Long(The University of Texas Southwestern Medical Center)
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