Prime editing of a pathogenic <i>Scn1a</i> allele ameliorates seizure phenotypes in a GEFS <sup>+</sup> mouse model

Lucas Kissling(University of Zurich), Gerald Schwank(ETH Zurich), Lukas Schmidheini(University of Zurich), Nicolas Mathis(University of Zurich), Péter István Kulcsár(University of Zurich), Hendrik Wildner, Konstantinos Kompotis, Francesca Pietrafesa(University of Zurich), András Tálas(University of Zurich), Desirée Böck(University of Zurich), Eleonora I. Ioannidi(University of Zurich), Xinyue Zhao(University of Zurich), Elina Villiger(University of Zurich), Matteo Ranucci(University of Zurich), Hanns Ulrich Zeilhofer(University of Zurich)
Science Translational Medicine
May 13, 2026
Cited by 0


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