GBA1 HDR Donor Vector Assembly v1Yu Chen(National Human Genome Research Institute)UnknownOctober 17, 202510.17504/protocols.io.ewov11m3ovr2/v1Cited by 0SaveCiteExport RISWatch citationsRelated PapersDevelopment of quantitative high-throughput screening assays to identify, validate, and optimize small-molecule stabilizers of misfolded β-glucocerebrosidase with therapeutic potential for Gaucher disease and Parkinson’s disease|bioRxiv (Cold Spring Harbor Laboratory)|2024|3Bidirectional regulation of glycoprotein nonmetastatic melanoma protein B by β-glucocerebrosidase deficiency in <i>GBA1</i> isogenic dopaminergic neurons from a patient with Gaucher disease and parkinsonism|bioRxiv (Cold Spring Harbor Laboratory)|2025|0