An optimized CRISPR-Cas12a genome-wide screen reveals PTPA phosphatase pathway in fetal hemoglobin silencing

Elizabeth A. Traxler(Children's Hospital of Philadelphia), Gerd A. Blobel(Children's Hospital of Philadelphia), Cheryl A. Keller(Pennsylvania State University), Eugene Khandros(Children's Hospital of Philadelphia), Belinda Giardine(Pennsylvania State University), Shuchen Yang(University of Pennsylvania), Kunhua Qin(Tianjin Medical University), Megan S. Saari(Children's Hospital of Philadelphia), Scott A. Peslak(Children's Hospital of Philadelphia), A. Josephine Thrasher(Children's Hospital of Philadelphia), Qingzhou Chen(University of Pennsylvania), Osheiza Abdulmalik(Children's Hospital of Philadelphia), Andy J. Minn(Memorial Sloan Kettering Cancer Center), Quynn Hotan(Children's Hospital of Philadelphia), Michelle Wang(University of Pennsylvania), R Hardison(Pennsylvania State University), Yue Shao(University of Pennsylvania), Junwei Shi(University of Pennsylvania), Chad A. Komar(University of Pennsylvania)
Blood
January 12, 2026
Cited by 1


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