A timeline of symptom onset and disease progression in CLN3 disease

Ineka T. Whiteman(EnergyAustralia (Australia)), Heather Adams(University of Rochester Medicine), Alexandra Johnson(Sydney Children's Hospital), John R. Østergaard(Aarhus University Hospital), Jonathan W. Mink(Science Take-Out (United States)), Jennifer Vermilion(University of Rochester Medicine), Amy Vierhile(University of Rochester Medicine), Erika F. Augustine(University of Rochester Medical Center), Heather Mason(Shared Services Canada), Aidan Bindoff(University of Tasmania), Angela Schulz(Universität Hamburg), Anthony L. Cook(University of Tasmania)
Orphanet Journal of Rare Diseases
January 7, 2026
Cited by 3


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