Genetic and Phenotypic Features of the Five Known Polyaminopathies: A Critical Narrative Review

Elizabeth VanSickle(Spectrum Health), Caleb Bupp(Spectrum Health), Sara M. Sarasua(Greenwood Genetic Center), Mary Jo Kutler(Parkinson's Foundation), Katharina Steindl(University of Zurich), Luigi Boccuto(Greenwood Genetic Center), André S. Bachmann(Michigan State University), Julianne Michael(Helen DeVos Children's Hospital), Angela Peron(University of Milan), Floris C. Hofstede(Wilhelmina Children's Hospital), Mythily Ganapathi(Columbia University Irving Medical Center), Susan K. Gilmour(Lankenau Institute for Medical Research), Tracy Lowe(Clemson University), Clément Prouteau(Northwestern University), Alban Ziegler(Columbia University Irving Medical Center), Teresa L. Mastracci(Indiana University Indianapolis), Surender Rajasekaran(Grand Rapids Community College), Víctor Faùndes(University of Manchester), Christopher Farrell(Clemson University), Charles E. Schwartz(Greenwood Genetic Center), Tracy Murray Stewart(Johns Hopkins University), Robert A. Casero(Harvard University), Teri L. Koerner(Parkinson's Foundation), Wendy K. Chung(Columbia University), Orrin Devinsky(New York University), Anthony E. Pegg(Penn State Milton S. Hershey Medical Center), Colleen Olson(New York University)
American Journal of Medical Genetics Part A
December 18, 2025
Cited by 1


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