Allogeneic hematopoietic cell transplantation in dyskeratosis congenita: Short and long- term outcome of 183 consecutive patients transplanted at EBMT centers

Fabiana Cacace(Duke University), Antonio M. Risitano(European Society for Blood and Marrow Transplantation), Krzysztof Kałwak(Poznan University of Medical Sciences), Bénédicte Neven(Université Paris-Panthéon-Assas), Constantijn J.M. Halkes(Radboud University Nijmegen), Alexey Maschan(Dmitry Rogachev National Research Center of Pediatric Hematology, Oncology and Immunology), Jean‐Hugues Dalle(Inserm), Polina Stepensky(Hebrew University of Jerusalem), Franco Locatelli(Bambino Gesù Children's Hospital), Filomena Pierri(Istituto Giannina Gaslini), Marta González‐Vicent(Hospital Infantil Universitario Niño Jesús), Adrían Alegre(Hospital Universitario de La Princesa), Dirk-Jan Eikema(European Society for Blood and Marrow Transplantation), Е. В. Скоробогатова(Russian Children's Clinical Hospital), Austin Kulasekararaj(King's College London), Maura Faraci(Istituto Giannina Gaslini), Sarah Lawson(Birmingham Children's Hospital), Cristina Díaz de Heredia(Universitat Autònoma de Barcelona), Franca Fagioli(Ospedale Regina Margherita), Ali Alahmari(King Faisal Specialist Hospital & Research Centre), Robert Wynn(Royal Manchester Children's Hospital), Brian Piepenbroek(Leiden University), Victoria Potter(University College Hospital), Maria Ester Bernardo(Unknown), Francesco Paolo Tambaro(The University of Texas MD Anderson Cancer Center), Flore Sicre-de-Fontbrune(Hôpital Saint-Louis), Joe Tuffnell(European Society for Blood and Marrow Transplantation), Laura Van Hussen-Daenen(University Medical Center Utrecht), Bénédicte Bruno(Centre Hospitalier Universitaire de Lille), Tayfun Güngör, Carlo Dufour(Istituto Giannina Gaslini), Mahmoud Aljurf(King Faisal Specialist Hospital & Research Centre), Gérard Michel(Hôpital de la Timone), Persis Amrolia(Great Ormond Street Hospital), Josu de la Fuente(Imperial College Healthcare NHS Trust), Adam Nelson(Sydney Children's Hospital), Francesca Fioredda(Istituto Giannina Gaslini)
Blood
November 3, 2025
Cited by 1


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