Generalizable features of pegRNA design for prime editing of inherited retinal diseases

Freya M. Patterson(University of Tasmania), Alex W. Hewitt(Lions Eye Institute), Anthony L. Cook(University of Tasmania), Mohd Khairul Nizam Mohd Khalid(University of Tasmania), Sandy Hung(Centre for Eye Research Australia), Minh Thuan Nguyen Tran(University of Tasmania), Kirsten A. Fairfax(University of Tasmania), Guei‐Sheung Liu(O'Brien Institute), Thomas Guinan(University of Tasmania), Rajendra KC(University of Illinois Urbana-Champaign)
Ophthalmic Genetics
November 9, 2025
Cited by 0


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