Base and Prime Editing for Inherited Retinal Diseases: Delivery Platforms, Safety, Efficacy, and Translational Perspectives

Haoliang Zhang(Shanghai Jiao Tong University), Tong Li(Pennsylvania State University), Yuxuan Li(Affiliated Hospital of Hangzhou Normal University), Xiaosa Li(Shanghai Jiao Tong University)
Pharmaceutics
October 30, 2025
Cited by 4


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