Prime editing for the investigation of aberrant splicing defect associated with a pathogenic PRPH2 variant

Bruna Lopes da Costa(Columbia University), Peter M. J. Quinn(University of Pennsylvania), Christopher D. Makinson(Stanford University), José Ronaldo Lima de Carvalho(University of Pennsylvania), Yi‐Ting Tsai(National Yang Ming Chiao Tung University), Siyuan Liu(University of California, San Francisco), Stephen H. Tsang(NewYork–Presbyterian Hospital), Salvatore Marco Caruso(NewYork–Presbyterian Hospital), Nicholas D. Nolan(NewYork–Presbyterian Hospital), Keith Theodore(University of Pennsylvania)
Molecular Therapy — Nucleic Acids
October 15, 2025
Cited by 3


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