Hepatocyte-targeted lipid nanoparticle for full-length ATP7B mRNA delivery in Wilson disease
Yukui Ma, Changyou Zhan(Shanghai Medical College of Fudan University), Kuan Jiang(Sun Yat-sen University), Bin Wang(Soochow University), Zhiwei Guo(Bristol-Myers Squibb (United States)), Songli Wang(Amgen (United States)), Kaisong Tian(Fudan University), Min Jae Yang(Yanbian University of Science and Technology), Weiping Wang(Hebei Medical University), Tianhao Ding(Fudan University)
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