Functional ability profiles in beta-propeller protein-associated neurodegeneration (BPAN)

Francesco Gavazzi(Children's Hospital of Philadelphia), Laura Adang(Children's Hospital of Philadelphia), Nivedita Thakur(Montreal Children's Hospital), Allan M. Glanzman(Boston Children's Hospital), Vanessa Smith(Ghent University Hospital), Stacy V. Cusack(Children's Hospital of Philadelphia), Sarah Woidill(Children's Hospital of Philadelphia), Samuel R. Pierce(Children's Hospital of Philadelphia), Julie Skorup(Children's Hospital of Philadelphia), Joseph Vithayathil, Emma K. Wiener(Children's Hospital of Philadelphia), Eric Yang(Children's Hospital of Philadelphia), Emma Kotes(Children's Hospital of Philadelphia), Kristy Pucci(Children's Hospital of Philadelphia), Abbas F. Jawad(Children's Hospital of Philadelphia), Todd Levy(Children's Hospital of Philadelphia), Holly Dubbs
Molecular Genetics and Metabolism
October 7, 2025
Cited by 0


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