Critical Functional Domains in Pediatric Onset TUBB4A-Related Leukodystrophy: A Clinical and Caregiver's Perspective
Francesco Gavazzi(Children's Hospital of Philadelphia), Adeline Vanderver(Children's Hospital of Philadelphia), Nicole I. Wolf(Emma Kinderziekenhuis), Ángeles García Cazorla(Hospital Sant Joan de Déu Barcelona), Anjana Sevagamoorthy(Children's Hospital of Philadelphia), Davide Tonduti, Ylenia Vaia, Sarah Woidill(Children's Hospital of Philadelphia), Brittany A. Charsar(Children's Hospital of Philadelphia), Virali Patel(Children's Hospital of Philadelphia), Jacqueline Erler(Children's Hospital of Philadelphia), Marjo S. van der Knaap(Amsterdam Neuroscience), Henry Houlden(Queen Mary University of London), Ariel Vincent(Children's Hospital of Philadelphia), Laura Adang(Children's Hospital of Philadelphia), Evangeline Wassmer(Birmingham Children's Hospital), Geneviève Bernard(McGill University)
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