Efficacy and safety of intravitreal rAAV2-ND4 therapy for Leber’s hereditary optic neuropathy

Libin Jiang(Beijing Tongren Hospital), Wenbin Wei(Beijing Tongren Hospital), Bin Li(Chinese Academy of Sciences), Su Xiao, Sitong Guo(The People's Hospital of Guangxi Zhuang Autonomous Region), Fei Wang(Zhejiang Chinese Medical University)
Eye
September 30, 2025
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