Nonclinical evaluation of renizgamglogene autogedtemcel for SCD and TDT

Eugenio Marco(Editas Medicine (United States)), Kai‐Hsin Chang(National Taiwan University), Ramya Viswanathan(Editas Medicine (United States)), Patricia Sousa(Editas Medicine (United States)), David K. Wood(University of Minnesota), Georgia Giannoukos(Editas Medicine (United States)), John A. Zuris(Howard Hughes Medical Institute), Mark C. Walters(UCSF Benioff Children's Hospital), Edouard De Dreuzy(Editas Medicine (United States)), Christopher J. Wilson, Tusneem Janoudi(Editas Medicine (United States)), Scott D. Hansen(University of Oregon), John F. Tisdale(National Heart Lung and Blood Institute), Jack Heath(Unknown), Gregory Gotta(Editas Medicine (United States))
Molecular Therapy
September 24, 2025
Cited by 3


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