Improvements in health-related quality of life in patients with severe sickle cell disease after exagamglogene autotemcel

Akshay Sharma(St. Jude Children's Research Hospital), Haydar Frangoul(Children’s Hospital at TriStar Centennial), Nanxin Li(Genomics Institute of the Novartis Research Foundation), Franco Locatelli(Bambino Gesù Children's Hospital), Lyndsay Molinari, Monica Bhatia(Columbia University Irving Medical Center), Wally R. Smith(Virginia Commonwealth University), Jaime Rubin(Vertex Pharmaceuticals (United States)), Kevin H.M. Kuo(University Health Network), Robert I. Liem(Lurie Children's Hospital), Michael J. Eckrich(Levine Children's Hospital), Tina Liu, Suzan Imren(Fred Hutch Cancer Center), Stephan A. Grupp(Children's Hospital of Philadelphia), William Hobbs(Vertex Pharmaceuticals (United States)), Laurence Dedeken(Université Libre de Bruxelles), Markus Y. Mapara(Sheba Medical Center), Puja Kohli(Brigham and Women's Hospital), Donna A. Wall(University of Manitoba)
Blood Advances
August 26, 2025
Cited by 4


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