Mesenchymal stromal cell infusions of umbilical cord-derived mesenchymal stromal cells in children with recessive dystrophic epidermolysis bullosa (MissionEB): a randomised, double-blind, placebo controlled, crossover, phase 3 trial with an internal phase 1 dose de-escalation phase
Maria L Bageta(Great Ormond Street Hospital for Children NHS Foundation Trust), Anna E. Martinez(National Health Service), Cindy Cooper(Department of Health and Social Care), Marie‐Louise Lovgren(Birmingham Women's Hospital), Muhammad Nadeem(University of Sargodha), Pratima Poudel(Birmingham Women's Hospital), Emily Turton(University of Sheffield), Matthew Bursnall(University of Sheffield), Katie Biggs(University of Sheffield), Malobi Ogboli(Birmingham Women's Hospital), Gabriela Petrof(Great Ormond Street Hospital), Diana Papaioannou(University of Sheffield), Paul Tappenden(University of Sheffield), Shamila Ditta(University of Sheffield), Rachel Glover(University of Sheffield), Pablo López Balboa(Great Ormond Street Hospital), John A. McGrath(King's College London), Steven A. Julious(University of Sheffield), Kate Hutchence(University of Sheffield), I. H. Wilson(University of Sheffield)
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