Improved outcome of HSCT in STAT1 gain-of-function disease following JAK inhibition bridging

Emilie P. Buddingh(Leiden University), Oscar De La Calle-Martin(Hospital de Sant Pau), Deepak Chellapandian(Johns Hopkins University), William Mitchell(Clemson University), Alexandra Laberko(Dmitry Rogachev National Research Center of Pediatric Hematology, Oncology and Immunology), Bénédicte Neven(Université Paris-Panthéon-Assas), Safa Barış(Marmara University), Lisa Forbes Satter(Baylor College of Medicine), Susan Farmand(Universität Hamburg), Mary Slatter(Royal Victoria Infirmary), Juan Carlos Aldave Becerra(Hospital Nacional Cayetano Heredia), Timothy Ronan Leahy(Children's Health Ireland at Crumlin), Caridad Martinez(Baylor College of Medicine), Michael H. Albert(LMU Klinikum), Jörn‐Sven Kühl(Charité - Universitätsmedizin Berlin), Ayça Kıykım(Marmara University), Shanmuganathan Chandrakasan(Emory University), Laura Martínez‐Martínez(Universitat Autònoma de Barcelona), Catharina Schütz(German Centre for Cardiovascular Research), Caroline A. Lindemans(University Medical Center Utrecht), Erik G. J. von Asmuth(Leiden University Medical Center), Jacques G. Rivière(Universitat Autònoma de Barcelona), Ami J. Shah(University of California, Los Angeles), Arjan C. Lankester(Leiden University Medical Center), Sara Şebnem Kılıç(Bursa Uludağ Üni̇versi̇tesi̇), Alice Chan(University of California, San Francisco), Troy R. Torgerson(Allen Institute for Immunology), Anders Fasth(University of Gothenburg), Renata Formánková(Charles University), Chaim M. Roifman(University of Toronto), Joseph H. Oved(Children's Hospital of Philadelphia), Jasmeen Dara(University of California, San Francisco), Eyal Grunebaum(University of Toronto), Su‐Wan Bianca Chan(KK Women's and Children's Hospital), Jennifer W. Leiding(Johns Hopkins University), Laura Alonso(Vall d'Hebron Hospital Universitari), Steven J. Keogh(Children's Hospital at Westmead), Linda Vong(Unknown), Emma Morris(University College London Hospitals NHS Foundation Trust), Maria Polacik(University Hospital Carl Gustav Carus)
Journal of Human Immunity
June 27, 2025
Cited by 11


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