A preclinical pig model of Angelman syndrome mirrors the early developmental trajectory of the human condition

Luke S. Myers(Texas A&M University), Scott V. Dindot(Ultragenyx Pharmaceutical (United States)), McKaela Hodge(Texas A&M University), Annalise Schlafer(Texas A&M University), Renan Sper(Mammoth Biosciences (United States)), Carol Knight(University of Surrey), Kevin Nash(University of South Florida), Jorge A. Piedrahita(North Carolina State University), Anne E. Anderson(Baylor College of Medicine), Sean Simpson(North Carolina State University), Thomas Jepp(University of Surrey), Jill L. Silverman(Mining Institute), Sarah Christian(Texas A&M University), Alasdair J. Taylor(University of Surrey), Laura Montes(Texas A&M University), David J. Segal(University of California, Davis), Kranti Konganti(Texas A&M University), Ashley Coffell(Institut thématique Génétique, génomique et bioinformatique), Daniela Ramos(Texas A&M University), Edwin J. Weeber(Society for Neuroscience), Wade Friedeck(Texas A&M University System), Ozair Habib(Texas A&M University), Morgan Matt(Texas A&M University), Bradley Revell(University of Surrey), Cristina C. Barreña(University of Surrey), William J. Murphy(Texas A&M University), Livia Schuller(Institut thématique Génétique, génomique et bioinformatique), Clint Taylor(Texas A&M University)
Proceedings of the National Academy of Sciences
July 21, 2025
Cited by 7


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