Clinically Important Endpoints in Individuals With Leukodystrophy: A Multisite Study
Emma Kotes(Children's Hospital of Philadelphia), Adeline Vanderver(Children's Hospital of Philadelphia), Russell D’Aiello(Children's Hospital of Philadelphia), Robert W. Grundmeier(Children's Hospital of Philadelphia), Kayla Muirhead(Children's Hospital of Philadelphia), Jordan Goodman(Kennedy Krieger Institute), Ali Fatemi(Kennedy Krieger Institute), Amy Waldman(Children's Hospital of Philadelphia), Mariko L. Bennett(Children's Hospital of Philadelphia), Sarah Woidill(Children's Hospital of Philadelphia), Amanda Nagy(Massachusetts General Hospital), Stephanie Keller(Children's Healthcare of Atlanta), Joshua L. Bonkowsky(Intermountain Healthcare), Francesco Gavazzi(Children's Hospital of Philadelphia), Keith Van Haren(Stanford University), Omar Sherbini(Children's Hospital of Philadelphia), Amena Smith Fine(Kennedy Krieger Institute), Jamie L. Fraser(Children's National), Lisa Emrick(Baylor College of Medicine), Mark Ramos(Children's Hospital of Philadelphia), Amy Pizzino(Children's Hospital of Philadelphia), Ashley Hackett(Emory University), Nicole Page(Massachusetts General Hospital), Johanna Schmidt(Counseling Center), Amina Khan(Children's Hospital of Philadelphia), Florian Eichler(Massachusetts General Hospital), D. Bernard Amos(National Institutes of Health), Justine Shults(Children's Hospital of Philadelphia), Jeilo Gauna(Lucile Packard Children's Hospital), Laura Adang(Children's Hospital of Philadelphia)
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