AAV gene therapy for autosomal recessive deafness 9: a single-arm trial

Jieyu Qi(Medical Protective), Renjie Chai(Medical Protective), Fangzhi Tan(Zhongda Hospital Southeast University), Yu Sun(Wuhan Prevention and Treatment Center for Occupational Diseases), Ling Lü(Nanjing Normal University), Xiaolong Fu(Qingdao University), Fan‐Gang Zeng(Chenzhou First People's Hospital), Maoli Duan(Karolinska University Hospital), Chang Tan(Cazenovia College), Dingjun Zha(The People's Hospital Tongling), Shanzhong Zhang(Cazenovia College), Cheng Cheng(St. Jude Children's Research Hospital), Lei Xu(Shandong University), Liyan Zhang(Zhongda Hospital Southeast University), Lulu Jiang(Jiangxi University of Science and Technology), Sijie Sun(Universitat Autònoma de Barcelona), Wenxiu Dong(Cazenovia College), Yicheng Lu(Nantong University), Xia Gao(Heilongjiang University of Science and Technology), Huaien Song(Fosun Pharma (China)), Yinyi Zhou(Zhongda Hospital Southeast University)
Nature Medicine
July 2, 2025
Cited by 33


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