AAV gene therapy for autosomal recessive deafness 9: a single-arm trial

Jieyu Qi(Beijing Institute of Technology), Renjie Chai(Nantong University), Fangzhi Tan(ShanghaiTech University), Yu Sun(Wuhan Prevention and Treatment Center for Occupational Diseases), Ling Lü(Nanjing Normal University), Xiaolong Fu(Fudan University Shanghai Cancer Center), Fan‐Gang Zeng(Renmin University of China), Maoli Duan(Karolinska University Hospital), Chang Tan(Cazenovia College), Dingjun Zha(Xijing Hospital), Shanzhong Zhang(Cazenovia College), Cheng Cheng(St. Jude Children's Research Hospital), Lei Xu(Shandong University), Liyan Zhang(Zhongda Hospital Southeast University), Lulu Jiang(Cazenovia College), Sijie Sun(Cazenovia College), Wenxiu Dong(Cazenovia College), Yicheng Lu(Second Military Medical University), Xia Gao(China Academy of Engineering Physics), Huaien Song(Fosun Pharma (China)), Yinyi Zhou(Zhongda Hospital Southeast University)
Nature Medicine
July 2, 2025
Cited by 33


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