First-in-human pharmacokinetic, safety, and preliminary efficacy of single- and multiple-dose FRSW117, a novel PEGylated recombinant factor VIII-Fc fusion protein with an extended half-life, in patients with severe hemophilia A

Feng Xue(Chinese Academy of Medical Sciences & Peking Union Medical College), Renchi Yang(Chinese Academy of Medical Sciences & Peking Union Medical College), Weizhi Chen(Genecast (China)), Haiying Hua(Jiangnan University), Yu Cao(Kunming University of Science and Technology), Chongyuan Xu(Nanfang Hospital), Yun Chen(Sun Yat-sen University), Ping Liu(Zhengzhou People's Hospital), Jing Sun(Qiqihar University), Qing Wen(Jinan Central Hospital), Xianqi Feng(Qingdao University), Shuxia Guo(Shihezi University)
Haematologica
June 12, 2025
Cited by 0


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