A mitochondrial disease model is generated and corrected using engineered base editors in rat zygotes

Liang Chen(Nanjing University of Information Science and Technology), Dali Li(East China Normal University), Changming Luan(East China Normal University), Meng Yuan(East China Normal University), Wensheng Wei(Peking University), Zongyi Yi(Peking University), Xinyuan Guo(East China Normal University), Lei Yang(Ministry of Agriculture), Yongmei Li(Tianjin Medical University), Mingyao Liu(Texas A&M Health Science Center), Honghui Han, Hao Huang(East China Normal University), Liangcai Gao(East China Normal University), Zhengxin Chen(Jiangsu Province Hospital), Mengjia Hong(East China Normal University)
Nature Biotechnology
June 3, 2025
Cited by 7


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