Operational Development and Launch of an Adaptive Platform Trial in Amyotrophic Lateral Sclerosis: Processes and Learnings From the First Four Regimens of the <scp>HEALEY ALS</scp> Platform Trial

Brittney Harkey(Massachusetts General Hospital), Jeremy M. Shefner(Creighton University), Gale Kittle(Barrow Neurological Institute), Lori B. Chibnik(Harvard University), Sabrina Paganoni(Harvard University), Elisa Giacomelli(Harvard University), Suma Babu(Harvard University), James D. Berry(Clinical Research Institute), Annette De Mattos(Massachusetts General Hospital), Sofia DiStefano(Massachusetts General Hospital), Merit Cudkowicz(Harvard University), Marianne Chase(Massachusetts General Hospital), Hong Yu(Massachusetts General Hospital), Derek D’Agostino(Massachusetts General Hospital), Jaclyn Pagliaro(Massachusetts General Hospital), Meghan Hall(Barrow Neurological Institute), Alexander V. Sherman(Massachusetts General Hospital), Kristin Drake(Massachusetts General Hospital), Andrew McGarry(Cooper Medical School of Rowan University), Margherita Torti, Catherine B. Small(Cornell University), Eric A. Macklin(Harvard University), Mariah Connolly(Barrow Neurological Institute), Courtney Igne(Massachusetts General Hospital), Cornelia Kamp(University of Rochester), Genevive Changkuon(Massachusetts General Hospital), Allison Bulat(Massachusetts General Hospital), Erica Scirocco(Massachusetts General Hospital), Eric Tustison(Massachusetts General Hospital), Lindsay Heyd(Massachusetts General Hospital)

Muscle & Nerve

May 26, 2025

Cited by 6

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