Healthcare utilization and disease burden in children with metachromatic leukodystrophy in Germany

Christiane Kehrer(University Children's Hospital Tübingen), Samuel Groeschel(University of Tübingen), Christa Raabe(University Children's Hospital Tübingen), Pascal Martin(Hertie Institute for Clinical Brain Research), Ingeborg Krägeloh‐Mann(University Children's Hospital Tübingen), Andrea Bevot(University Children's Hospital Tübingen)
Orphanet Journal of Rare Diseases
May 23, 2025
Cited by 1


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