A multifunction murine <i>Col4a1</i> allele reveals potential gene therapy parameters for Gould syndrome

Mao Mao(University of California, San Francisco), Douglas B. Gould(University of California, San Francisco), Megan Smith(University of California, San Francisco), Yien–Ming Kuo(University of California, San Francisco), Xiaowei Wang(University of California, San Francisco), Cassandre Labelle‐Dumais(University of California, San Francisco), Carlie N. Abdala(University of California, San Francisco), Yoshihiro Ishikawa(University of California, San Francisco), Uma Bhagwat Gaffney(University of California, San Francisco), Matthew D. Lebedev(University of California, San Francisco), William Paradee(University of Iowa)
The Journal of Cell Biology
March 21, 2025
Cited by 7


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