Porous Silicon Nanoneedles Efficiently Deliver Adenine Base Editor to Correct a Recurrent Pathogenic <i>COL7A1</i> Variant in Recessive Dystrophic Epidermolysis Bullosa

Salman Ahmad Mustfa(King's College London), Ciro Chiappini(King's College London), Ningjia Sun(King's College London), Paweł Karpiński(Wroclaw Medical University), Łukasz Łaczmański(Ludwik Hirszfeld Institute of Immunology and Experimental Therapy), Marija Dimitrievska(King's College London), John A. McGrath(St. Thomas Hospital), Katarzyna Balon(Ludwik Hirszfeld Institute of Immunology and Experimental Therapy), Cong Wang(King's College London), Chenlei Gu(King's College London)
Advanced Materials
March 12, 2025
Cited by 9


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