Safety and efficacy of a fitusiran antithrombin-based dose regimen in people with hemophilia A or B: the ATLAS-OLE study

Guy Young(Children's Hospital of Los Angeles), Yuqian Shen(Sanofi (United States)), Robert Klamroth(Klinikum im Friedrichshain), Steven W. Pipe(University of Michigan), Savita Rangarajan(Guy's and St Thomas' NHS Foundation Trust), Laurel A. Menapace(National Institutes of Health), Alok Srivastava(M.J.P. Rohilkhand University), Ming‐Ching Shen(National Taiwan University Hospital), Gili Kenet(Sheba Medical Center), Tadashi Matsushita(Nagoya University Hospital), Bülent Zülfikar(Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico), Flora Peyvandi(University of Milan), Chuanwu Zhang(AVEO Oncology (United States)), Kaan Kavaklı(Ege University), Marja Puurunen(Synlogic (United States)), Huyen Tran(The Alfred Hospital), Jing Sun(Qiqihar University), Marek Demissie(Sanofi (United States)), Chur-Woo You(Eulji University)
Blood
March 7, 2025
Cited by 38


Related Papers