AAV9-mediated MYBPC3 gene therapy with optimized expression cassette enhances cardiac function and survival in MYBPC3 cardiomyopathy models
Amara Greer-Short(Virginia Commonwealth University), Laura M. Lombardi(Howard Hughes Medical Institute), Jaclyn J. Ho, Marie Cho, Frank Jing, Jun Liu, Ana Budan, Charles Feathers, Elena C. Leon, Emilee Easter, Tawny Neal Qureshi, William S. Prince, Konor von Kraut, Jonathan H. Tsui, Timothy Hoey, Stephanie Steltzer, Olga Cisne-Thompson, Justin Wong(The University of Sydney), Jin Yang(Rapt Therapeutics (United States)), Rishikesan Chandrakumar, Chris Alleyne-Levy, Anna Greenwood, Samantha Jones, Ze Cheng, Whittemore G. Tingley(Howard Hughes Medical Institute), Neshel Rodriguez, Jianmin Lin, Tae Won Chung, Kathryn N. Ivey
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