Highly efficient in vivo hematopoietic stem cell transduction using an optimized self-complementary adeno-associated virus

Carsten T. Charlesworth(Stanford University), Hiromitsu Nakauchi(Japan Science and Technology Agency), Sicong Wang(Stanford University), Agnieszka Czechowicz(Stanford University), M. Kyle Cromer(University of California, San Francisco), Amanda M. Dudek(Stanford University), Adam C. Wilkinson(Wellcome/MRC Cambridge Stem Cell Institute), Carla Dib(Stanford University), Shota Homma(Stanford University), Kyomi J. Igarashi(Harvard University), Fabian P. Suchy(Stanford University), Alvaro Amorin(Stanford University), Sriram Vaidyanathan(Nationwide Children's Hospital), Anais K. Amaya(Stanford University), Yusuke Nakauchi(Stanford University), Masashi Miyauchi(California Institute for Regenerative Medicine), Tze-Kai Tan(Stanford University)
Molecular Therapy — Methods & Clinical Development
February 21, 2025
Cited by 3


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