Highly efficient in vivo hematopoietic stem cell transduction using an optimized self-complementary adeno-associated virus

Carsten T. Charlesworth(Stanford University), Hiromitsu Nakauchi(University of Tsukuba), Sicong Wang(Uppsala University), Agnieszka Czechowicz(Boston Children's Hospital), M. Kyle Cromer(Gladstone Institutes), Amanda M. Dudek(Stanford University), Adam C. Wilkinson(Wellcome/MRC Cambridge Stem Cell Institute), Carla Dib(Stanford University), Shota Homma(Stanford University), Kyomi J. Igarashi(California Institute for Regenerative Medicine), Fabian P. Suchy(California Institute for Regenerative Medicine), Alvaro Amorin(Stanford University), Sriram Vaidyanathan(Nationwide Children's Hospital), Anais K. Amaya(Stanford University), Yusuke Nakauchi(Stanford University), Masashi Miyauchi(California Institute for Regenerative Medicine), Tze-Kai Tan(Stanford University)
Molecular Therapy — Methods & Clinical Development
February 21, 2025
Cited by 3


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