The natural history of variable subtypes in pediatric-onset TUBB4A-related leukodystrophy
Francesco Gavazzi(Children's Hospital of Philadelphia), Adeline Vanderver(Children's Hospital of Philadelphia), Laura Adang(Children's Hospital of Philadelphia), Geneviève Bernard(McGill University), Francesco Nicita(Sapienza University of Rome), Ivailo Tournev(Université Paris-Sud), Cas Simons(Garvan Institute of Medical Research), Nicole I. Wolf(Emma Kinderziekenhuis), Kayla Muirhead(Children's Hospital of Philadelphia), Hiroshi Doi(RIKEN Center for Brain Science), Asako Takanohashi(Children's Hospital of Philadelphia), Anjana Sevagamoorthy(Children's Hospital of Philadelphia), Davide Tonduti, Sarah Woidill(Children's Hospital of Philadelphia), Ángeles García‐Cazorla(Hospital Sant Joan de Déu Barcelona), Brittany A. Charsar(Children's Hospital of Philadelphia), Virali Patel(Children's Hospital of Philadelphia), Helia Toutounchi(McGill University), Enrico Bertini(Bambino Gesù Children's Hospital), Jacqueline Erler(Children's Hospital of Philadelphia), Marjo S. van der Knaap(Amsterdam Neuroscience), Joshua L. Bonkowsky(Intermountain Healthcare), Daniel R. Carvalho(Areté Associates (United States)), Meredith Sanchez‐Castillo(Translational Genomics Research Institute), Menno D. Stellingwerff(Vrije Universiteit Amsterdam), Guy Helman(Murdoch Children's Research Institute), Albena Jordanova(University of Antwerp), Amytice Mirchi(McGill University), Nancy J. Clegg(Texas Scottish Rite Hospital for Children), Dan Williams(Adaptix (United Kingdom)), Henry Houlden(Queen Mary University of London), Teodora Chamova(Alexandrovska Hospital), Naomichi Matsumoto(Yokohama City University), Evangeline Wassmer(Birmingham Children's Hospital), Amy Pizzino(Children's Hospital of Philadelphia), Johanna Schmidt(Counseling Center), Mauricio R. Delgado(The University of Texas Southwestern Medical Center), Michelle Teng, Kelsee Meyerhoffer(University of Utah), Justine Shults(Children's Hospital of Philadelphia), Miyatake Satoko(Yokohama City University), Eline M. Hamilton(Amsterdam University Medical Centers)
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