Single-AAV CRISPR editing of skeletal muscle in non-human primates with NanoCas, an ultracompact nuclease

Benjamin J. Rauch(Mammoth Biosciences (United States)), Lucas B. Harrington(Mammoth Biosciences (United States)), Jason Lin(Chiba Cancer Center), Maggie Bobbin(Mammoth Biosciences (United States)), Renan Sper(Mammoth Biosciences (United States)), Will Wright(Mammoth Biosciences (United States)), Alexander Neckelmann(Mammoth Biosciences (United States)), Ymer M. Bjornson(San Jose State University), Shiaki A. Minami(Mammoth Biosciences (United States)), James P. Broughton(Mammoth Biosciences (United States)), Aaron DeLoughery(Mammoth Biosciences (United States)), Christopher A. Schmitt(Mammoth Biosciences (United States)), Sara Ansaloni(Mammoth Biosciences (United States)), Bohong Zhang(Unknown), Mark A. DeWitt(Mammoth Biosciences (United States)), Alyssa Sancio(Mammoth Biosciences (United States)), Keith Abe(Mammoth Biosciences (United States)), Ning Chai(Mammoth Biosciences (United States)), Stepan Tymoshenko(Mammoth Biosciences (United States)), Matan Drory Retwitzer(Mammoth Biosciences (United States)), Sean Chen(Rutgers, The State University of New Jersey), P. M. Narendra(Mammoth Biosciences (United States)), Siming Xu(Mammoth Biosciences (United States)), David Paez Espino(Mammoth Biosciences (United States)), Subhadra Jayaraman Rukmini(Mammoth Biosciences (United States)), Sahana Somaiah(Mammoth Biosciences (United States)), Sophia Yunanda(Mammoth Biosciences (United States)), Clarissa Scholes(Mammoth Biosciences (United States)), Megan Masnaghetti(Mammoth Biosciences (United States)), Shravanti K. Suresh(Mammoth Biosciences (United States))
bioRxiv (Cold Spring Harbor Laboratory)
January 30, 2025
Cited by 6


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