Audiology assessment of participants in CAMPSIITE®, a phase I/II/III study of investigational RGX-121 in neuronopathic MPS II

Nidal Boulos, Paulo Falabella, Patricia Roush(University of North Carolina at Chapel Hill), Dawn Phillips(ProterixBio (United States)), Laura Rosa Pisani(Regenxbio (United States))
Molecular Genetics and Metabolism
January 30, 2025
Cited by 0


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