iPSC-derived hepatocytes accurately recapitulate population diversity in alpha-1-antitrypsin deficiency and offer a novel <i>in vitro</i> model for large-scale drug efficacy screening studies

Carlos Gómez Gil(Babraham Institute), Nikolaos Nikolaou(Babraham Institute)
bioRxiv (Cold Spring Harbor Laboratory)
January 23, 2025
Cited by 1


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