Targeted allele-specific FGFR2 knockdown via human recombinant ferritin nanoparticles for personalized treatment of Crouzon syndrome

Federica Tiberio(Università Cattolica del Sacro Cuore), Wanda Lattanzi(Università Cattolica del Sacro Cuore)
Molecular Therapy — Nucleic Acids
December 12, 2024
Cited by 6


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