Durable Clinical Benefits with Exagamglogene Autotemcel for Transfusion-Dependent β-Thalassemia

Franco Locatelli(Bambino Gesù Children's Hospital), Haydar Frangoul(Children’s Hospital at TriStar Centennial), Donna A. Wall(University of Manitoba), Mattia Algeri(Bambino Gesù Children's Hospital), Leorah Ross, Ben Carpenter(The Royal Free Hospital), Roland Meisel(Heinrich Heine University Düsseldorf), Sujit Sheth(Columbia University Irving Medical Center), Antonis Kattamis, Bo Tong(AbbVie (United States)), Peter Lang(STZ eyetrial), Amanda M. Li(BC Children's Hospital), Maria Domenica Cappellini(Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico), Kevin H.M. Kuo(University Health Network), Robert I. Liem(Lurie Children's Hospital), Ami J. Shah(University of California, Los Angeles), Yael Bobruff(Vertex Pharmaceuticals (United States)), Hayley Merkeley(University of British Columbia), Stephan A. Grupp(Children's Hospital of Philadelphia), Gang Xu(University of Michigan), Selim Corbacioglu(Unknown), Janet L. Kwiatkowski(Children's Hospital of Philadelphia), William Hobbs(Vertex Pharmaceuticals (United States)), Puja Kohli(Brigham and Women's Hospital), Josu de la Fuente(Imperial College Healthcare NHS Trust), Joachim Rupprecht(University of Tübingen), Markus Y. Mapara(Sheba Medical Center)
Blood
November 5, 2024
Cited by 4


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