Human glyoxylate metabolism revisited: New insights pointing to multi‐organ involvement with implications for <scp>siRNA</scp>‐based therapies in primary hyperoxaluria

R. J. A. Wanders(Emma Kinderziekenhuis), Sander F. Garrelfs(Emma Kinderziekenhuis), Jaap W. Groothoff(University of Amsterdam), Eduardo Salido(Universidad de La Laguna), Lisa J. Deesker(Emma Kinderziekenhuis)
Journal of Inherited Metabolic Disease
November 24, 2024
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