Systematic empirical evaluation of individual base editing targets: validating therapeutic targets in <i>USH2A</i> and comparison of methods

Yuki Tachida(Massachusetts Eye and Ear Infirmary), Jason Comander(Massachusetts Eye and Ear Infirmary)

bioRxiv (Cold Spring Harbor Laboratory)

October 3, 2024

10.1101/2024.10.02.615422

Cited by 0

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Systematic empirical evaluation of individual base editing targets: Validating therapeutic targets in USH2A and comparison of methods

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