Effects of oral sepiapterin on blood Phe concentration in a broad range of patients with phenylketonuria (APHENITY): results of an international, phase 3, randomised, double-blind, placebo-controlled trial
Ania C. Muntau(Universität Hamburg), Nicola Longo(University of California, Los Angeles), Fatih Süheyl Ezgü(Gazi University), Ida Vanessa Döederlein Schwartz(Universidade Federal do Rio Grande do Sul), Melissa Lah(Indiana University School of Medicine), Drago Bratkovic(Women's and Children's Hospital), Lali Margvelashvili(National Cancer Center of Georgia), Ertuğrul Kıykım(Istanbul University-Cerrahpaşa), Roberto T. Zori(University of Florida), Jaume Campistol Plana(Hospital Sant Joan de Déu Barcelona), Amaya Bélanger-Quintana(Hospital Universitario Ramón y Cajal), Allan M. Lund(Copenhagen University Hospital), Laura Guilder(University of Toronto), Anupam Chakrapani(Great Ormond Street Hospital), Halise Neslihan Mungan(Cukurova University), Arlindo Guimas(Centro Hospitalar do Porto), Ixiu del Carmen Cabrales Guerra(Universidad Panamericana), Anita MacDonald(Birmingham Women’s and Children’s NHS Foundation Trust), Kimberly Ingalls(PTC Therapeutics (United States)), Neil Smith(PTC Therapeutics (United States)), Ania C Muntau(Universität Hamburg), Nicola Longo(University of California, Los Angeles), Fatih Ezgu(Gazi University), Ida Vanessa D Schwartz(Universidade Federal do Rio Grande do Sul), Melissa Lah(Indiana University School of Medicine), Drago Bratkovic(Women's and Children's Hospital), Lali Margvelashvili(National Cancer Center of Georgia), Ertugrul Kiykim(Istanbul University-Cerrahpaşa), Roberto Zori(University of Florida), Jaume Campistol Plana(Hospital Sant Joan de Déu Barcelona), Amaya Bélanger-Quintana(Hospital Universitario Ramón y Cajal), Allan Lund(Copenhagen University Hospital), Laura Guilder(University of Toronto), Anupam Chakrapani(Great Ormond Street Hospital), Halise Neslihan Mungan(Cukurova University), Arlindo Guimas(Centro Hospitalar do Porto), Ixiu del Carmen Cabrales Guerra(Universidad Panamericana), Anita MacDonald(Birmingham Women’s and Children’s NHS Foundation Trust), Kimberly Ingalls(PTC Therapeutics (United States)), Stephanie Sacharow, Maria Avanise Yumi Minami, Frank Rutsch, Michel Tchan, Heidi Peters, Aneal Khan, Suresh Vijay, Thomas Opladen, Hope Northrup, Anabela Oliveira, François Feillet, Dodo Agladze, Catalina Hughes, Alexandra Larkin, Sarah Milner, Lan Gao, Rochelle Greenbaum, Zhenming Zhao, Neil Smith(PTC Therapeutics (United States))
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