Adeno-associated virus serotype 9 antibodies in neonates and young children: Seroprevalence and kinetics

Rudolf W. van Olden(Rotkreuzklinikum München), Christophe Lo Bianco(Rotkreuzklinikum München), Keith W. Dilly(Baxalta (United States)), M. Savelieva(Novartis (Switzerland)), Siyan Xu(Novartis (United States)), Aloys Tijsma(Rotterdam University of Applied Sciences), Carel van Baalen(Rotterdam University of Applied Sciences), Harsh Sharma(Rotkreuzklinikum München), Nayla Mumneh(Novartis (United States))
Molecular Therapy — Methods & Clinical Development
September 21, 2024
Cited by 9Open Access
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Abstract

= 18 patients). The model-based estimation of the AAV9-Ab IgG average half-life was 41 (95% CI, 38-44) days. Based on visualization, 200 ELISA units/mL was a reasonable approximate for the 1:50 titer threshold. In conclusion, initially elevated titers ≥1:100 in newborn patients declined with age. The new quantitative ELISA may allow for quantification of time to threshold for AAV9-Ab IgG retesting for onasemnogene abeparvovec treatment, leading to treatment as early as possible for patients with SMA.


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