Newborn Screening and Presymptomatic Treatment of Metachromatic Leukodystrophy

Lucia Laugwitz(University Children's Hospital Tübingen), Samuel Groeschel(University of Tübingen), Thomas P. Mechtler, Nils Janzen(Medizinische Hochschule Hannover), Petra Oliva, Michaela Döring(University Children's Hospital Tübingen), Pascal Martin(Hertie Institute for Clinical Brain Research), Marcus Weitz(University Children's Hospital Tübingen), David C. Kasper(Mayo Clinic), Stefanie Beck‐Woedl(University of Tübingen), Johannes H. Schulte(German Cancer Research Center), Andrew Shenker, Peter Lang(STZ eyetrial), Joachim Janda(Heidelberg University), Charlotte E. Teunissen(Amsterdam Neuroscience), Charlotte Chanson, Mirko M. Essing, Berthold Streubel(Medical University of Vienna), Andrea-Romana Kasper(Medical University of Vienna), Hendrik Rosewich(University Children's Hospital Tübingen), Friederike Bürger(Heidelberg University), Tobias B. Haack(Technical University of Munich)
New England Journal of Medicine
September 18, 2024
Cited by 20


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