Antisense Oligonucleotide STK-002 Increases OPA1 in Retina and Improves Mitochondrial Function in Autosomal Dominant Optic Atrophy Cells

Aditya Venkatesh(Beam Therapeutics (United States)), Jeff Hoger(Beam Therapeutics (United States))
Nucleic Acid Therapeutics
September 12, 2024
Cited by 11


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