Restoration of peripheral neuropathy in Fabry mice via intrathecal administration of an adeno-associated virus vector encoding mGLA cDNA

Takashi Higuchi(Kyoto University), Hiroshi Kobayashi(Mayo Clinic in Arizona), Fusao Kato(Jikei University School of Medicine), Toya Ohashi(Jikei University School of Medicine), Yohta Shimada(Jikei University School of Medicine), Yukari Takahashi(Jikei University School of Medicine)
Molecular Genetics and Metabolism
July 27, 2024
Cited by 5


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