Retinal cells derived from patients with DRAM2-dependent CORD21 dystrophy exhibit key lysosomal enzyme deficiency and lysosomal content accumulation

Rozaliya Tsikandelova(Newcastle University), Majlinda Lako(Newcastle University), Jennifer Haggarty(University of Glasgow), Μαρία Γεωργίου(Newcastle University), Florence Burté(Newcastle University), Dean Hallam(Newcastle University), Lyle Armstrong(Newcastle University), Birthe Dorgau(Newcastle University), Chunbo Yang(Xinjiang Medical University), Edvinas Cerniauskas(Center for Environmental Health), Rodrigo Cerna-Chavez(Newcastle University), Robert Atkinson(Newcastle University), Tracey Davies(Newcastle University), Phil Whitfield(University of Glasgow), Viktor Korolchuk(Newcastle University), Pavel Palmowski(Newcastle University), David H. Steel(Newcastle University), Martin McKibbin(University of Leeds), Jacquelyn Bond(University of Leeds), Eldo Galo(Newcastle University), Marzena Kurzawa‐Akanbi(Newcastle University)
Stem Cell Reports
July 3, 2024
Cited by 5


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